Your generous donation will impact the lives of patients through PALS’ support of Dr. Mary Kay Koenig, MD and her team at the Center for the Treatment of Pediatric Neurodegenerative Diseases, and the Leigh Syndrome International Consortium, among other initiatives.
Specifically, over the next year, PALS’ funding priorities include:
-TRiaLS: The International Registry for Leigh Syndrome. Funded by PALS and managed by Dr. Mary Kay Koenig's team, TRiaLS is a highly secure patient registry that quickly connects patients to clinicians and researchers seeking treatments and cures for Leigh syndrome. There are currently more than 160 patients from around the world, including the United States, Australia, Canada, Great Britain, India, Japan, Venezuela, Romania, Croatia and Poland on the registry.
- Leigh Syndrome International Consortium. PALS has partnered with the United Mitochondrial Disease Foundation (UMDF), MitoCon (Italy), Mitochondrial Disease Foundation (Australia), and the Lily Foundation (Great Britain) to bring together the world's leading clinicians and researchers to improve diagnosis, develop better treatments and hopefully a cure, and optimize clinical care for Leigh syndrome patients. Funds gifted by our organizations are being used for research grants, a natural history study and more.
- Independent Research. PALS granted 50,000 USD total to two research teams that are exploring therapeutic treatments for Leigh syndrome patients. The research projects were identified through PALS’ first-ever Request for Proposals (RFP) seeking independent research that needed funding for the final push to advance a project from the “benchtop to the bedside” with the goal to positively impact patient care in the near future. The awardees were announced in January 2022. Read more.
Tax deductible donations can be made below, by calling Lindsey Klingensmith at 713-248-8782, or by mailing a check to PO Box 7057, Houston, TX 77248.